[Elsevier] Long-term reversal of Duchenne muscular dystrophy via circular arRNA-guided exon skipping in monkeys and humans

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journal:Cell

Authors:Wenting Guo; Huixian Tang; Zongyi Yi; Ting Zhang; Pengfei Yuan; Cuijin Wang; Shuaiwei Ren; Xiwen Chang; Jiwu Ren; Wei Tang; Wenjie Sun; Jie Liu; Ying Yu; Zhiwei Lu; Hongyan Shen; Zexuan Yi; Yanxia Zhao; Gangbin Tang; Junyuan Han; Wenzhi Zhang; Haoyue Liu; Xueqing Sun; Yongjian Zhang; Cui Zhang; Yuming Wu; Ling Yang; Feng Han; Yichao Xu; Liang Qu; Xinyan Sun; Jiwen Wang; Weizhi Ji; Yongchang Chen; Wensheng Wei

Published date:2026-6-

DOI:10.1016/j.cell.2026.05.030

PDF link:https://www.sciencedirect.com/sc ... 092867426005891/pdf

Article link:https://doi.org/10.1016/j.cell.2026.05.030

Article Source:Elsevier BV


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